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3. Advances in the treatment of inherited metabolic diseases. Desnick RJ; Grabowski GA Adv Hum Genet; 1981; 11():281-369. PubMed ID: 6115548 [No Abstract] [Full Text] [Related]
4. Experimental enzyme replacement in genetic and other disorders. Weissmann G Hosp Pract; 1976 Sep; 11(9):49-58. PubMed ID: 1071086 [TBL] [Abstract][Full Text] [Related]
5. The future for gene therapy--a reevaluation. Friedmann T Ann N Y Acad Sci; 1976; 265():141-52. PubMed ID: 1066080 [No Abstract] [Full Text] [Related]
6. [Therapeutic perspectives in hereditary metabolic diseases]. Royer P Rev Med Suisse Romande; 1972 Jun; 92(6):419-28. PubMed ID: 4637780 [No Abstract] [Full Text] [Related]
7. [The treatment of congenital errors of metabolism]. Baldellou A An Esp Pediatr; 1997 Dec; 47(6):563-7. PubMed ID: 9575114 [No Abstract] [Full Text] [Related]
8. Diagnosis and management of inborn errors of metabolism. Wraith JE Arch Dis Child; 1989 Oct; 64(10 Spec No):1410-5. PubMed ID: 2686556 [No Abstract] [Full Text] [Related]
9. Inborn errors of metabolism: principles and their applications. Pinksy L Can Med Assoc J; 1972 Mar; 106(6):677 passim. PubMed ID: 4551928 [No Abstract] [Full Text] [Related]
10. [Medical applications and therapeutic prospects deduced from knowledge in molecular pathology]. Royer P Biochimie; 1972; 54(5):789-99. PubMed ID: 4347398 [No Abstract] [Full Text] [Related]
11. [Gene therapy and animal model for inborn errors of metabolism]. Yamamura K Tanpakushitsu Kakusan Koso; 1988 Apr; 33(5):475-80. PubMed ID: 3270852 [No Abstract] [Full Text] [Related]
13. [Possibilities and limits of the treatment of genetic metabolic defects]. Theile H Z Gesamte Inn Med; 1981 Jun; 36(11):338-41. PubMed ID: 6946644 [TBL] [Abstract][Full Text] [Related]
14. Is there treatment for "genetic" disease? Scriver CR; Treacy EP Mol Genet Metab; 1999 Oct; 68(2):93-102. PubMed ID: 10527662 [No Abstract] [Full Text] [Related]
15. [Gene therapy for the treatment of inborn errors of metabolism]. Pérez-López J Med Clin (Barc); 2014 Jun; 142(12):549-53. PubMed ID: 23932565 [TBL] [Abstract][Full Text] [Related]
16. Gene therapy for inborn errors of liver metabolism. Brunetti-Pierri N; Lee B Mol Genet Metab; 2005; 86(1-2):13-24. PubMed ID: 16154372 [TBL] [Abstract][Full Text] [Related]
17. Progress toward improved therapies for inborn errors of metabolism. Ginocchio VM; Brunetti-Pierri N Hum Mol Genet; 2016 Apr; 25(R1):R27-35. PubMed ID: 26443595 [TBL] [Abstract][Full Text] [Related]
18. [Scientific rationale for the use of vitamins in the prophylactic and therapeutic purposes. Report 2. Vitamin deficit as a factor complicating the course disease and reducing the efficiency of medical and prophylaxis measures]. Spirichev VB Vopr Pitan; 2011; 80(1):4-13. PubMed ID: 21574463 [TBL] [Abstract][Full Text] [Related]
19. Hepatocyte transplantation for inborn errors of metabolism. Burlina AB J Inherit Metab Dis; 2004; 27(3):373-83. PubMed ID: 15190195 [TBL] [Abstract][Full Text] [Related]
20. [Enzyme replacement: recognition and transport of lysosomal enzymes]. González Noriega A Bol Estud Med Biol; 1983; 32(7-8 Suppl 1):209-17. PubMed ID: 6543638 [No Abstract] [Full Text] [Related] [Next] [New Search]