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63. Bone marrow stem cell-based gene transfer in a mouse model for metachromatic leukodystrophy: effects on visceral and nervous system disease manifestations. Matzner U; Hartmann D; Lüllmann-Rauch R; Coenen R; Rothert F; Månsson JE; Fredman P; D'Hooge R; De Deyn PP; Gieselmann V Gene Ther; 2002 Jan; 9(1):53-63. PubMed ID: 11850723 [TBL] [Abstract][Full Text] [Related]
64. [Hereditary diseases related to a disorder in the breakdown of carbohydrate-containing compounds]. Vidershaĭn GIa Usp Sovrem Biol; 1974; 77(3):434-51. PubMed ID: 4278594 [No Abstract] [Full Text] [Related]
65. Biochemical approaches to the nosology of nervous system defects, III. Menkes JH Birth Defects Orig Artic Ser; 1971 Feb; 7(1):37-41. PubMed ID: 5006214 [TBL] [Abstract][Full Text] [Related]
66. Tay-Sachs disease-causing mutations and neutral polymorphisms in the Hex A gene. Myerowitz R Hum Mutat; 1997; 9(3):195-208. PubMed ID: 9090523 [TBL] [Abstract][Full Text] [Related]
67. Enzyme replacement in feline GM2 gangliosidosis: catabolic effects of human beta-hexosaminidase A. Rattazzi MC; Appel AM; Baker HJ Prog Clin Biol Res; 1982; 94():213-20. PubMed ID: 6214798 [No Abstract] [Full Text] [Related]
68. Successful transduction of oligodendrocytes and restoration of arylsulfatase A deficiency in metachromatic leukodystrophy fibroblasts using an adenovirus vector. Ohashi T; Watabe K; Sato Y; Saito I; Barranger JA; Eto Y Gene Ther; 1995 Sep; 2(7):443-9. PubMed ID: 7584122 [TBL] [Abstract][Full Text] [Related]
69. [Diagnosis of lysosomal storage diseases using ultrastructural studies and biopsies of the conjunctiva]. Libert J; Danis P Bull Mem Soc Fr Ophtalmol; 1981; 93():144-50. PubMed ID: 6809088 [No Abstract] [Full Text] [Related]
70. [Pathogenetic studies of abnormal brain development (author's transl)]. Herschkowitz N; Wiesmann U; Vassella F Schweiz Rundsch Med Prax; 1975 Sep; 64(35):1120-4. PubMed ID: 1215297 [No Abstract] [Full Text] [Related]
71. [Magnetic resonance imaging in Tay-Sachs disease]. Ozawa H; Sugai K; Sasaki S No To Shinkei; 1995 Aug; 47(8):800-1. PubMed ID: 7546928 [No Abstract] [Full Text] [Related]
72. Enzyme replacement therapy for the sphingolipidoses. Brady RO; Pentchev PG; Gal AE; Hibbert SR; Quirk JM; Mook GE; Kusiak JW; Tallman JF; Dekaban AS Adv Exp Med Biol; 1976; 68():523-32. PubMed ID: 820173 [No Abstract] [Full Text] [Related]
73. Emerging strategies for the treatment of hereditary metabolic storage disorders. Brady RO Rejuvenation Res; 2006; 9(2):237-44. PubMed ID: 16706651 [TBL] [Abstract][Full Text] [Related]
74. Bone marrow transplantation for metabolic diseases. Parkman R; Crooks G; Kohn DB; Lenarsky C; Weinberg K Cancer Treat Res; 1995; 76():87-96. PubMed ID: 7577346 [No Abstract] [Full Text] [Related]