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2. Gene Therapy in Fanconi Anemia: A Matter of Time, Safety and Gene Transfer Tool Efficiency. Verhoeyen E; Roman-Rodriguez FJ; Cosset FL; Levy C; Rio P Curr Gene Ther; 2017; 16(5):297-308. PubMed ID: 28067165 [TBL] [Abstract][Full Text] [Related]
3. Gene therapy for canine alpha-L-iduronidase deficiency: in utero adoptive transfer of genetically corrected hematopoietic progenitors results in engraftment but not amelioration of disease. Lutzko C; Omori F; Abrams-Ogg AC; Shull R; Li L; Lau K; Ruedy C; Nanji S; Gartley C; Dobson H; Foster R; Kruth S; Dubé ID Hum Gene Ther; 1999 Jun; 10(9):1521-32. PubMed ID: 10395377 [TBL] [Abstract][Full Text] [Related]
4. Gene therapy for haematopoietic and lymphoid disorders. Kohn DB Clin Exp Immunol; 1997 Jan; 107 Suppl 1():54-7. PubMed ID: 9020937 [TBL] [Abstract][Full Text] [Related]
5. Stem Cell Genetic Therapy for Fanconi Anemia - A New Hope. Hanenberg H; Roellecke K; Wiek C Curr Gene Ther; 2017; 16(5):309-320. PubMed ID: 28067166 [TBL] [Abstract][Full Text] [Related]
6. Gene transfer into haemopoietic cells. Stocking C; Baum C Baillieres Clin Haematol; 1997 Sep; 10(3):445-65. PubMed ID: 9421610 [TBL] [Abstract][Full Text] [Related]
7. Gene transfer. A potential approach to gene therapy for sickle cell disease. Bank A; Markowitz D; Lerner N Ann N Y Acad Sci; 1989; 565():37-43. PubMed ID: 2672970 [TBL] [Abstract][Full Text] [Related]
8. Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study. Ferrua F; Cicalese MP; Galimberti S; Giannelli S; Dionisio F; Barzaghi F; Migliavacca M; Bernardo ME; Calbi V; Assanelli AA; Facchini M; Fossati C; Albertazzi E; Scaramuzza S; Brigida I; Scala S; Basso-Ricci L; Pajno R; Casiraghi M; Canarutto D; Salerio FA; Albert MH; Bartoli A; Wolf HM; Fiori R; Silvani P; Gattillo S; Villa A; Biasco L; Dott C; Culme-Seymour EJ; van Rossem K; Atkinson G; Valsecchi MG; Roncarolo MG; Ciceri F; Naldini L; Aiuti A Lancet Haematol; 2019 May; 6(5):e239-e253. PubMed ID: 30981783 [TBL] [Abstract][Full Text] [Related]
9. Ten years of gene therapy for primary immune deficiencies. Aiuti A; Roncarolo MG Hematology Am Soc Hematol Educ Program; 2009; ():682-9. PubMed ID: 20008254 [TBL] [Abstract][Full Text] [Related]
10. Gene transfer into human hematopoietic progenitor cells: a review of current clinical protocols. Brenner MK J Hematother; 1993; 2(1):7-17. PubMed ID: 7522875 [TBL] [Abstract][Full Text] [Related]
11. Long-term in vitro correction of alpha-L-iduronidase deficiency (Hurler syndrome) in human bone marrow. Fairbairn LJ; Lashford LS; Spooncer E; McDermott RH; Lebens G; Arrand JE; Arrand JR; Bellantuono I; Holt R; Hatton CE; Cooper A; Besley GT; Wraith JE; Anson DS; Hopwood JJ; Dexter TM Proc Natl Acad Sci U S A; 1996 Mar; 93(5):2025-30. PubMed ID: 8700879 [TBL] [Abstract][Full Text] [Related]
12. The contribution of marker gene studies to hemopoietic stem cell therapies. Brenner MK Stem Cells; 1995 Sep; 13(5):453-61. PubMed ID: 8528094 [TBL] [Abstract][Full Text] [Related]
13. Gene transfer into hematopoietic cells: progress, problems and prospects. Dilber MS Turk J Pediatr; 1998; 40(3):307-36. PubMed ID: 9763896 [TBL] [Abstract][Full Text] [Related]
14. Hematopoietic stem cell gene transfer for the treatment of hemoglobin disorders. Persons DA Hematology Am Soc Hematol Educ Program; 2009; ():690-7. PubMed ID: 20008255 [TBL] [Abstract][Full Text] [Related]
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16. Gene transfer into murine hematopoietic stem cells and bone marrow stromal cells. Luskey BD; Lim B; Apperley JF; Orkin SH; Williams DA Ann N Y Acad Sci; 1990; 612():398-406. PubMed ID: 2291566 [TBL] [Abstract][Full Text] [Related]
17. Lentiviral hematopoietic cell gene therapy for X-linked adrenoleukodystrophy. Cartier N; Hacein-Bey-Abina S; Bartholomae CC; Bougnères P; Schmidt M; Kalle CV; Fischer A; Cavazzana-Calvo M; Aubourg P Methods Enzymol; 2012; 507():187-98. PubMed ID: 22365775 [TBL] [Abstract][Full Text] [Related]
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19. Gene transfer into hematopoietic progenitor and stem cells: progress and problems. Dunbar CE; Emmons RV Stem Cells; 1994 Nov; 12(6):563-76. PubMed ID: 7881358 [TBL] [Abstract][Full Text] [Related]
20. Development of HIV vectors for anti-HIV gene therapy. Poeschla E; Corbeau P; Wong-Staal F Proc Natl Acad Sci U S A; 1996 Oct; 93(21):11395-9. PubMed ID: 8876146 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]