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8. [Gene therapy of Gaucher's and Fabry's diseases: current status and prospects]. Fabrega S; Lehn P J Soc Biol; 2002; 196(2):175-81. PubMed ID: 12360746 [TBL] [Abstract][Full Text] [Related]
9. The lipidoses: morphologic changes in the nervous system in Gaucher's disease, GM2 gangliosidoses and Niemann-Pick disease. Arey JB Ann Clin Lab Sci; 1975; 5(6):475-88. PubMed ID: 812418 [TBL] [Abstract][Full Text] [Related]
10. An appraisal of human trials in enzyme replacement therapy of genetic diseases. Tager JM; Hamers MN; Schram AW; Van den Bergh FA; Rietra PJ; Loonen C; Koster JF; Slee R Birth Defects Orig Artic Ser; 1980; 16(1):343-59. PubMed ID: 6778527 [No Abstract] [Full Text] [Related]
11. Enzyme replacement therapy for lysosomal storage disorders: successful transition from concept to clinical practice. Sly WS Mo Med; 2004; 101(2):100-4. PubMed ID: 15119106 [TBL] [Abstract][Full Text] [Related]
12. Diagnostic and therapeutic applications of sphingolipid hydrolyzing enzymes. Brady RO Curr Top Cell Regul; 1985; 26():39-50. PubMed ID: 3935381 [No Abstract] [Full Text] [Related]
13. Enzyme replacement therapy for the sphingolipidoses. Brady RO; Pentchev PG; Gal AE; Hibbert SR; Quirk JM; Mook GE; Kusiak JW; Tallman JF; Dekaban AS Adv Exp Med Biol; 1976; 68():523-32. PubMed ID: 820173 [No Abstract] [Full Text] [Related]