149 related articles for article (PubMed ID: 8177709)
1. Gene therapy for lysosomal disorders.
Naffakh N; Bohl D; Salvetti A; Moullier P; Danos O; Heard JM
Nouv Rev Fr Hematol (1978); 1994; 36 Suppl 1():S11-6. PubMed ID: 8177709
[TBL] [Abstract][Full Text] [Related]
2. Correction of lysosomal storage in the liver and spleen of MPS VII mice by implantation of genetically modified skin fibroblasts.
Moullier P; Bohl D; Heard JM; Danos O
Nat Genet; 1993 Jun; 4(2):154-9. PubMed ID: 8348154
[TBL] [Abstract][Full Text] [Related]
3. Delivery of a retroviral vector expressing human beta-glucuronidase to the liver and spleen decreases lysosomal storage in mucopolysaccharidosis VII mice.
Gao C; Sands MS; Haskins ME; Ponder KP
Mol Ther; 2000 Sep; 2(3):233-44. PubMed ID: 10985954
[TBL] [Abstract][Full Text] [Related]
4. High level expression and export of beta-glucuronidase from murine mucopolysaccharidosis VII cells corrected by a double-copy retrovirus vector.
Wolfe JH; Kyle JW; Sands MS; Sly WS; Markowitz DG; Parente MK
Gene Ther; 1995 Jan; 2(1):70-8. PubMed ID: 7712336
[TBL] [Abstract][Full Text] [Related]
5. Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer.
Wolfe JH; Sands MS; Barker JE; Gwynn B; Rowe LB; Vogler CA; Birkenmeier EH
Nature; 1992 Dec 24-31; 360(6406):749-53. PubMed ID: 1465145
[TBL] [Abstract][Full Text] [Related]
6. Gene transfer of low levels of beta-glucuronidase corrects hepatic lysosomal storage in a large animal model of mucopolysaccharidosis VII.
Wolfe JH; Sands MS; Harel N; Weil MA; Parente MK; Polesky AC; Reilly JJ; Hasson C; Weimelt S; Haskins ME
Mol Ther; 2000 Dec; 2(6):552-61. PubMed ID: 11124056
[TBL] [Abstract][Full Text] [Related]
7. Cross-correction of beta-glucuronidase deficiency by retroviral vector-mediated gene transfer.
Taylor RM; Wolfe JH
Exp Cell Res; 1994 Oct; 214(2):606-13. PubMed ID: 7925654
[TBL] [Abstract][Full Text] [Related]
8. [Gene therapy in lysosomal diseases].
Moullier P; Salvetti A; Bohl D; Danos O; Heard JM
C R Seances Soc Biol Fil; 1996; 190(1):45-51. PubMed ID: 8881268
[TBL] [Abstract][Full Text] [Related]
9. In utero fetal liver cell transplantation without toxic irradiation alleviates lysosomal storage in mice with mucopolysaccharidosis type VII.
Barker JE; Deveau S; Lessard M; Hamblen N; Vogler C; Levy B
Blood Cells Mol Dis; 2001; 27(5):861-73. PubMed ID: 11783949
[TBL] [Abstract][Full Text] [Related]
10. Widespread biochemical correction of murine mucopolysaccharidosis type VII pathology by liver hydrodynamic plasmid delivery.
Richard M; Arfi A; Seguin J; Gandolphe C; Scherman D
Gene Ther; 2009 Jun; 16(6):746-56. PubMed ID: 19357715
[TBL] [Abstract][Full Text] [Related]
11. In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using nonprimate lentiviral vectors.
Stein CS; Kang Y; Sauter SL; Townsend K; Staber P; Derksen TA; Martins I; Qian J; Davidson BL; McCray PB
Mol Ther; 2001 Jun; 3(6):850-6. PubMed ID: 11407898
[TBL] [Abstract][Full Text] [Related]
12. Brain transplantation of genetically modified bone marrow stromal cells corrects CNS pathology and cognitive function in MPS VII mice.
Sakurai K; Iizuka S; Shen JS; Meng XL; Mori T; Umezawa A; Ohashi T; Eto Y
Gene Ther; 2004 Oct; 11(19):1475-81. PubMed ID: 15295619
[TBL] [Abstract][Full Text] [Related]
13. Brain transplantation of genetically engineered human neural stem cells globally corrects brain lesions in the mucopolysaccharidosis type VII mouse.
Meng XL; Shen JS; Ohashi T; Maeda H; Kim SU; Eto Y
J Neurosci Res; 2003 Oct; 74(2):266-77. PubMed ID: 14515356
[TBL] [Abstract][Full Text] [Related]
14. Retrovirus-mediated transfer of the human alpha-L-iduronidase cDNA into human hematopoietic progenitor cells leads to correction in trans of Hurler fibroblasts.
Huang MM; Wong A; Yu X; Kakkis E; Kohn DB
Gene Ther; 1997 Nov; 4(11):1150-9. PubMed ID: 9425437
[TBL] [Abstract][Full Text] [Related]
15. Treatment of murine mucopolysaccharidosis type VII by syngeneic bone marrow transplantation in neonates.
Sands MS; Barker JE; Vogler C; Levy B; Gwynn B; Galvin N; Sly WS; Birkenmeier E
Lab Invest; 1993 Jun; 68(6):676-86. PubMed ID: 8515654
[TBL] [Abstract][Full Text] [Related]
16. Retroviral cDNA transfer to the RPE: stable expression and modification of metabolism.
Ray J; Wolfe JH; Aguirre GD; Haskins ME
Invest Ophthalmol Vis Sci; 1998 Aug; 39(9):1658-66. PubMed ID: 9699555
[TBL] [Abstract][Full Text] [Related]
17. Cloning of the canine beta-glucuronidase cDNA, mutation identification in canine MPS VII, and retroviral vector-mediated correction of MPS VII cells.
Ray J; Bouvet A; DeSanto C; Fyfe JC; Xu D; Wolfe JH; Aguirre GD; Patterson DF; Haskins ME; Henthorn PS
Genomics; 1998 Mar; 48(2):248-53. PubMed ID: 9521879
[TBL] [Abstract][Full Text] [Related]
18. In vivo delivery of human alpha-L-iduronidase in mice implanted with neo-organs.
Salvetti A; Moullier P; Cornet V; Brooks D; Hopwood JJ; Danos O; Heard JM
Hum Gene Ther; 1995 Sep; 6(9):1153-9. PubMed ID: 8527473
[TBL] [Abstract][Full Text] [Related]
19. Treatment of lysosomal storage disease in MPS VII mice using a recombinant adeno-associated virus.
Watson GL; Sayles JN; Chen C; Elliger SS; Elliger CA; Raju NR; Kurtzman GJ; Podsakoff GM
Gene Ther; 1998 Dec; 5(12):1642-9. PubMed ID: 10023443
[TBL] [Abstract][Full Text] [Related]
20. Active site mutant transgene confers tolerance to human beta-glucuronidase without affecting the phenotype of MPS VII mice.
Sly WS; Vogler C; Grubb JH; Zhou M; Jiang J; Zhou XY; Tomatsu S; Bi Y; Snella EM
Proc Natl Acad Sci U S A; 2001 Feb; 98(5):2205-10. PubMed ID: 11226217
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
