BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

329 related articles for article (PubMed ID: 8200966)

  • 1. Enzyme replacement therapy for murine mucopolysaccharidosis type VII.
    Sands MS; Vogler C; Kyle JW; Grubb JH; Levy B; Galvin N; Sly WS; Birkenmeier EH
    J Clin Invest; 1994 Jun; 93(6):2324-31. PubMed ID: 8200966
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Enzyme replacement with recombinant beta-glucuronidase in murine mucopolysaccharidosis type VII: impact of therapy during the first six weeks of life on subsequent lysosomal storage, growth, and survival.
    Vogler C; Sands MS; Levy B; Galvin N; Birkenmeier EH; Sly WS
    Pediatr Res; 1996 Jun; 39(6):1050-4. PubMed ID: 8725268
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Enzyme replacement in murine mucopolysaccharidosis type VII: neuronal and glial response to beta-glucuronidase requires early initiation of enzyme replacement therapy.
    Vogler C; Levy B; Galvin NJ; Thorpe C; Sands MS; Barker JE; Baty J; Birkenmeier EH; Sly WS
    Pediatr Res; 1999 Jun; 45(6):838-44. PubMed ID: 10367775
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Widespread correction of lysosomal storage following intrahepatic injection of a recombinant adeno-associated virus in the adult MPS VII mouse.
    Sferra TJ; Backstrom K; Wang C; Rennard R; Miller M; Hu Y
    Mol Ther; 2004 Sep; 10(3):478-91. PubMed ID: 15336648
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Murine mucopolysaccharidosis type VII: the impact of therapies on the clinical course and pathology in a murine model of lysosomal storage disease.
    Vogler C; Sands MS; Galvin N; Levy B; Thorpe C; Barker J; Sly WS
    J Inherit Metab Dis; 1998 Aug; 21(5):575-86. PubMed ID: 9728337
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Treatment of a lysosomal storage disease, mucopolysaccharidosis VII, with microencapsulated recombinant cells.
    Ross CJ; Bastedo L; Maier SA; Sands MS; Chang PL
    Hum Gene Ther; 2000 Oct; 11(15):2117-27. PubMed ID: 11044913
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Treatment of murine mucopolysaccharidosis type VII by syngeneic bone marrow transplantation in neonates.
    Sands MS; Barker JE; Vogler C; Levy B; Gwynn B; Galvin N; Sly WS; Birkenmeier E
    Lab Invest; 1993 Jun; 68(6):676-86. PubMed ID: 8515654
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Murine mucopolysaccharidosis type VII: long term therapeutic effects of enzyme replacement and enzyme replacement followed by bone marrow transplantation.
    Sands MS; Vogler C; Torrey A; Levy B; Gwynn B; Grubb J; Sly WS; Birkenmeier EH
    J Clin Invest; 1997 Apr; 99(7):1596-605. PubMed ID: 9120003
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Enzyme replacement with recombinant beta-glucuronidase in the newborn mucopolysaccharidosis type VII mouse.
    Vogler C; Sands M; Higgins A; Levy B; Grubb J; Birkenmeier EH; Sly WS
    Pediatr Res; 1993 Dec; 34(6):837-40. PubMed ID: 8108204
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Enzyme replacement therapy improves reproductive performance in mucopolysaccharidosis type VII mice but does not prevent postnatal losses.
    Soper BW; Pung AW; Vogler CA; Grubb JH; Sly WS; Barker JE
    Pediatr Res; 1999 Feb; 45(2):180-6. PubMed ID: 10022587
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Lentiviral-mediated gene therapy results in sustained expression of β-glucuronidase for up to 12 months in the gus(mps/mps) and up to 18 months in the gus(tm(L175F)Sly) mouse models of mucopolysaccharidosis type VII.
    Derrick-Roberts AL; Pyragius CE; Kaidonis XM; Jackson MR; Anson DS; Byers S
    Hum Gene Ther; 2014 Sep; 25(9):798-810. PubMed ID: 25003807
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Enzyme replacement therapy for murine mucopolysaccharidosis type VII leads to improvements in behavior and auditory function.
    O'Connor LH; Erway LC; Vogler CA; Sly WS; Nicholes A; Grubb J; Holmberg SW; Levy B; Sands MS
    J Clin Invest; 1998 Apr; 101(7):1394-400. PubMed ID: 9525982
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Early onset of lysosomal storage disease in a murine model of mucopolysaccharidosis type VII: undegraded substrate accumulates in many tissues in the fetus and very young MPS VII mouse.
    Vogler C; Levy B; Galvin N; Lessard M; Soper B; Barker J
    Pediatr Dev Pathol; 2005; 8(4):453-62. PubMed ID: 16222480
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Widespread biochemical correction of murine mucopolysaccharidosis type VII pathology by liver hydrodynamic plasmid delivery.
    Richard M; Arfi A; Seguin J; Gandolphe C; Scherman D
    Gene Ther; 2009 Jun; 16(6):746-56. PubMed ID: 19357715
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Comparison of ventricular and intravenous lentiviral-mediated gene therapy for murine MPS VII.
    Bielicki J; McIntyre C; Anson DS
    Mol Genet Metab; 2010 Dec; 101(4):370-82. PubMed ID: 20864369
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Vestronidase alfa: Recombinant human β-glucuronidase as an enzyme replacement therapy for MPS VII.
    Cadaoas J; Boyle G; Jungles S; Cullen S; Vellard M; Grubb JH; Jurecka A; Sly W; Kakkis E
    Mol Genet Metab; 2020 May; 130(1):65-76. PubMed ID: 32192868
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Bone marrow transplantation has a significant effect on enzyme levels and storage of glycosaminoglycans in tissues and in isolated hepatocytes of mucopolysaccharidosis type VII mice.
    Poorthuis BJ; Romme AE; Willemsen R; Wagemaker G
    Pediatr Res; 1994 Aug; 36(2):187-93. PubMed ID: 7970933
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Neonatal retroviral vector-mediated hepatic gene therapy reduces bone, joint, and cartilage disease in mucopolysaccharidosis VII mice and dogs.
    Mango RL; Xu L; Sands MS; Vogler C; Seiler G; Schwarz T; Haskins ME; Ponder KP
    Mol Genet Metab; 2004 May; 82(1):4-19. PubMed ID: 15110316
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.
    Daly TM; Okuyama T; Vogler C; Haskins ME; Muzyczka N; Sands MS
    Hum Gene Ther; 1999 Jan; 10(1):85-94. PubMed ID: 10022533
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Syngeneic bone marrow transplantation reduces the hearing loss associated with murine mucopolysaccharidosis type VII.
    Sands MS; Erway LC; Vogler C; Sly WS; Birkenmeier EH
    Blood; 1995 Sep; 86(5):2033-40. PubMed ID: 7655032
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 17.