BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

329 related articles for article (PubMed ID: 8200966)

  • 21. Behavior and therapeutic efficacy of beta-glucuronidase-positive mononuclear phagocytes in a murine model of mucopolysaccharidosis type VII.
    Freeman BJ; Roberts MS; Vogler CA; Nicholes A; Hofling AA; Sands MS
    Blood; 1999 Sep; 94(6):2142-50. PubMed ID: 10477745
    [TBL] [Abstract][Full Text] [Related]  

  • 22. Gene therapy for murine mucopolysaccharidosis type VII.
    Sands MS; Wolfe JH; Birkenmeier EH; Barker JE; Vogler C; Sly WS; Okuyama T; Freeman B; Nicholes A; Muzyczka N; Chang PL; Axelrod HR
    Neuromuscul Disord; 1997 Jul; 7(5):352-60. PubMed ID: 9267850
    [TBL] [Abstract][Full Text] [Related]  

  • 23. Evaluation of pathological manifestations of disease in mucopolysaccharidosis VII mice after neonatal hepatic gene therapy.
    Xu L; Mango RL; Sands MS; Haskins ME; Ellinwood NM; Ponder KP
    Mol Ther; 2002 Dec; 6(6):745-58. PubMed ID: 12498771
    [TBL] [Abstract][Full Text] [Related]  

  • 24. Overcoming the blood-brain barrier with high-dose enzyme replacement therapy in murine mucopolysaccharidosis VII.
    Vogler C; Levy B; Grubb JH; Galvin N; Tan Y; Kakkis E; Pavloff N; Sly WS
    Proc Natl Acad Sci U S A; 2005 Oct; 102(41):14777-82. PubMed ID: 16162667
    [TBL] [Abstract][Full Text] [Related]  

  • 25. In utero fetal liver cell transplantation without toxic irradiation alleviates lysosomal storage in mice with mucopolysaccharidosis type VII.
    Barker JE; Deveau S; Lessard M; Hamblen N; Vogler C; Levy B
    Blood Cells Mol Dis; 2001; 27(5):861-73. PubMed ID: 11783949
    [TBL] [Abstract][Full Text] [Related]  

  • 26. Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse.
    Sferra TJ; Qu G; McNeely D; Rennard R; Clark KR; Lo WD; Johnson PR
    Hum Gene Ther; 2000 Mar; 11(4):507-19. PubMed ID: 10724030
    [TBL] [Abstract][Full Text] [Related]  

  • 27. Active site mutant transgene confers tolerance to human beta-glucuronidase without affecting the phenotype of MPS VII mice.
    Sly WS; Vogler C; Grubb JH; Zhou M; Jiang J; Zhou XY; Tomatsu S; Bi Y; Snella EM
    Proc Natl Acad Sci U S A; 2001 Feb; 98(5):2205-10. PubMed ID: 11226217
    [TBL] [Abstract][Full Text] [Related]  

  • 28. A novel model of murine mucopolysaccharidosis type VII due to an intracisternal a particle element transposition into the beta-glucuronidase gene: clinical and pathologic findings.
    Vogler C; Levy B; Galvin N; Sands MS; Birkenmeier EH; Sly WS; Barker J
    Pediatr Res; 2001 Mar; 49(3):342-8. PubMed ID: 11228259
    [TBL] [Abstract][Full Text] [Related]  

  • 29. Gene transfer of low levels of beta-glucuronidase corrects hepatic lysosomal storage in a large animal model of mucopolysaccharidosis VII.
    Wolfe JH; Sands MS; Harel N; Weil MA; Parente MK; Polesky AC; Reilly JJ; Hasson C; Weimelt S; Haskins ME
    Mol Ther; 2000 Dec; 2(6):552-61. PubMed ID: 11124056
    [TBL] [Abstract][Full Text] [Related]  

  • 30. Brain transplantation of genetically modified bone marrow stromal cells corrects CNS pathology and cognitive function in MPS VII mice.
    Sakurai K; Iizuka S; Shen JS; Meng XL; Mori T; Umezawa A; Ohashi T; Eto Y
    Gene Ther; 2004 Oct; 11(19):1475-81. PubMed ID: 15295619
    [TBL] [Abstract][Full Text] [Related]  

  • 31. Biochemical evidence for superior correction of neuronal storage by chemically modified enzyme in murine mucopolysaccharidosis VII.
    Huynh HT; Grubb JH; Vogler C; Sly WS
    Proc Natl Acad Sci U S A; 2012 Oct; 109(42):17022-7. PubMed ID: 23027951
    [TBL] [Abstract][Full Text] [Related]  

  • 32. Delivery of a retroviral vector expressing human beta-glucuronidase to the liver and spleen decreases lysosomal storage in mucopolysaccharidosis VII mice.
    Gao C; Sands MS; Haskins ME; Ponder KP
    Mol Ther; 2000 Sep; 2(3):233-44. PubMed ID: 10985954
    [TBL] [Abstract][Full Text] [Related]  

  • 33. Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer.
    Bosch A; Perret E; Desmaris N; Trono D; Heard JM
    Hum Gene Ther; 2000 May; 11(8):1139-50. PubMed ID: 10834616
    [TBL] [Abstract][Full Text] [Related]  

  • 34. Acidic amino acid tag enhances response to enzyme replacement in mucopolysaccharidosis type VII mice.
    MontaƱo AM; Oikawa H; Tomatsu S; Nishioka T; Vogler C; Gutierrez MA; Oguma T; Tan Y; Grubb JH; Dung VC; Ohashi A; Miyamoto K; Orii T; Yoneda Y; Sly WS
    Mol Genet Metab; 2008 Jun; 94(2):178-89. PubMed ID: 18359257
    [TBL] [Abstract][Full Text] [Related]  

  • 35. Treatment of lysosomal storage disease in MPS VII mice using a recombinant adeno-associated virus.
    Watson GL; Sayles JN; Chen C; Elliger SS; Elliger CA; Raju NR; Kurtzman GJ; Podsakoff GM
    Gene Ther; 1998 Dec; 5(12):1642-9. PubMed ID: 10023443
    [TBL] [Abstract][Full Text] [Related]  

  • 36. Correction of lysosomal storage in the liver and spleen of MPS VII mice by implantation of genetically modified skin fibroblasts.
    Moullier P; Bohl D; Heard JM; Danos O
    Nat Genet; 1993 Jun; 4(2):154-9. PubMed ID: 8348154
    [TBL] [Abstract][Full Text] [Related]  

  • 37. Numerous transcriptional alterations in liver persist after short-term enzyme-replacement therapy in a murine model of mucopolysaccharidosis type VII.
    Woloszynek JC; Roberts M; Coleman T; Vogler C; Sly W; Semenkovich CF; Sands MS
    Biochem J; 2004 Apr; 379(Pt 2):461-9. PubMed ID: 14705966
    [TBL] [Abstract][Full Text] [Related]  

  • 38. Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.
    Frisella WA; O'Connor LH; Vogler CA; Roberts M; Walkley S; Levy B; Daly TM; Sands MS
    Mol Ther; 2001 Mar; 3(3):351-8. PubMed ID: 11273777
    [TBL] [Abstract][Full Text] [Related]  

  • 39. AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice.
    Hennig AK; Ogilvie JM; Ohlemiller KK; Timmers AM; Hauswirth WW; Sands MS
    Mol Ther; 2004 Jul; 10(1):106-16. PubMed ID: 15233947
    [TBL] [Abstract][Full Text] [Related]  

  • 40. Gene therapy ameliorates cardiovascular disease in dogs with mucopolysaccharidosis VII.
    Sleeper MM; Fornasari B; Ellinwood NM; Weil MA; Melniczek J; O'Malley TM; Sammarco CD; Xu L; Ponder KP; Haskins ME
    Circulation; 2004 Aug; 110(7):815-20. PubMed ID: 15289379
    [TBL] [Abstract][Full Text] [Related]  

    [Previous]   [Next]    [New Search]
    of 17.