These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

147 related articles for article (PubMed ID: 8527473)

  • 1. In vivo delivery of human alpha-L-iduronidase in mice implanted with neo-organs.
    Salvetti A; Moullier P; Cornet V; Brooks D; Hopwood JJ; Danos O; Heard JM
    Hum Gene Ther; 1995 Sep; 6(9):1153-9. PubMed ID: 8527473
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Retrovirus-mediated transfer of the human alpha-L-iduronidase cDNA into human hematopoietic progenitor cells leads to correction in trans of Hurler fibroblasts.
    Huang MM; Wong A; Yu X; Kakkis E; Kohn DB
    Gene Ther; 1997 Nov; 4(11):1150-9. PubMed ID: 9425437
    [TBL] [Abstract][Full Text] [Related]  

  • 3. α- L-iduronidase gene-based therapy using the phiC31 system to treat mucopolysaccharidose type I mice.
    Stilhano RS; Martin PK; de Melo SM; Samoto VY; Peres GB; da Silva Michelacci YM; da Silva FH; Pereira VG; D'Almeida V; da Cruz AT; Jasiulionis MG; Han SW
    J Gene Med; 2015; 17(1-2):1-13. PubMed ID: 25597593
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Limited transgene immune response and long-term expression of human alpha-L-iduronidase in young adult mice with mucopolysaccharidosis type I by liver-directed gene therapy.
    Di Domenico C; Di Napoli D; Gonzalez Y Reyero E; Lombardo A; Naldini L; Di Natale P
    Hum Gene Ther; 2006 Nov; 17(11):1112-21. PubMed ID: 17044753
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Effect of neonatal administration of a retroviral vector expressing alpha-L-iduronidase upon lysosomal storage in brain and other organs in mucopolysaccharidosis I mice.
    Chung S; Ma X; Liu Y; Lee D; Tittiger M; Ponder KP
    Mol Genet Metab; 2007 Feb; 90(2):181-92. PubMed ID: 16979922
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Treatment of the mouse model of mucopolysaccharidosis I with retrovirally transduced bone marrow.
    Zheng Y; Rozengurt N; Ryazantsev S; Kohn DB; Satake N; Neufeld EF
    Mol Genet Metab; 2003 Aug; 79(4):233-44. PubMed ID: 12948739
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Improved retroviral vector design results in sustained expression after adult gene therapy in mucopolysaccharidosis I mice.
    Herati RS; Ma X; Tittiger M; Ohlemiller KK; Kovacs A; Ponder KP
    J Gene Med; 2008 Sep; 10(9):972-82. PubMed ID: 18613275
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Gene therapy for lysosomal disorders.
    Naffakh N; Bohl D; Salvetti A; Moullier P; Danos O; Heard JM
    Nouv Rev Fr Hematol (1978); 1994; 36 Suppl 1():S11-6. PubMed ID: 8177709
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Enzymatic correction and cross-correction of mucopolysaccharidosis type I fibroblasts by adeno-associated virus-mediated transduction of the alpha-L-iduronidase gene.
    Hartung SD; Reddy RG; Whitley CB; McIvor RS
    Hum Gene Ther; 1999 Sep; 10(13):2163-72. PubMed ID: 10498248
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Improvements in mucopolysaccharidosis I mice after adult retroviral vector-mediated gene therapy with immunomodulation.
    Ma X; Liu Y; Tittiger M; Hennig A; Kovacs A; Popelka S; Wang B; Herati R; Bigg M; Ponder KP
    Mol Ther; 2007 May; 15(5):889-902. PubMed ID: 17311010
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Intranasal Adeno-Associated Virus Mediated Gene Delivery and Expression of Human Iduronidase in the Central Nervous System: A Noninvasive and Effective Approach for Prevention of Neurologic Disease in Mucopolysaccharidosis Type I.
    Belur LR; Temme A; Podetz-Pedersen KM; Riedl M; Vulchanova L; Robinson N; Hanson LR; Kozarsky KF; Orchard PJ; Frey WH; Low WC; McIvor RS
    Hum Gene Ther; 2017 Jul; 28(7):576-587. PubMed ID: 28462595
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Correction of lysosomal storage in the liver and spleen of MPS VII mice by implantation of genetically modified skin fibroblasts.
    Moullier P; Bohl D; Heard JM; Danos O
    Nat Genet; 1993 Jun; 4(2):154-9. PubMed ID: 8348154
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Gene therapy for a mucopolysaccharidosis type I murine model with lentiviral-IDUA vector.
    Di Domenico C; Villani GR; Di Napoli D; Reyero EG; Lombardo A; Naldini L; Di Natale P
    Hum Gene Ther; 2005 Jan; 16(1):81-90. PubMed ID: 15703491
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Correction of metabolic, craniofacial, and neurologic abnormalities in MPS I mice treated at birth with adeno-associated virus vector transducing the human alpha-L-iduronidase gene.
    Hartung SD; Frandsen JL; Pan D; Koniar BL; Graupman P; Gunther R; Low WC; Whitley CB; McIvor RS
    Mol Ther; 2004 Jun; 9(6):866-75. PubMed ID: 15194053
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Retroviral vector design studies toward hematopoietic stem cell gene therapy for mucopolysaccharidosis type I.
    Pan D; Aronovich E; McIvor RS; Whitley CB
    Gene Ther; 2000 Nov; 7(21):1875-83. PubMed ID: 11110421
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Identification and molecular characterization of alpha-L-iduronidase mutations present in mucopolysaccharidosis type I patients undergoing enzyme replacement therapy.
    Yogalingam G; Guo XH; Muller VJ; Brooks DA; Clements PR; Kakkis ED; Hopwood JJ
    Hum Mutat; 2004 Sep; 24(3):199-207. PubMed ID: 15300847
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Identification and characterization of the molecular lesion causing mucopolysaccharidosis type I in cats.
    He X; Li CM; Simonaro CM; Wan Q; Haskins ME; Desnick RJ; Schuchman EH
    Mol Genet Metab; 1999 Jun; 67(2):106-12. PubMed ID: 10356309
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Correction of mucopolysaccharidosis type I fibroblasts by retroviral-mediated transfer of the human alpha-L-iduronidase gene.
    Anson DS; Bielicki J; Hopwood JJ
    Hum Gene Ther; 1992 Aug; 3(4):371-9. PubMed ID: 1525210
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Recombinant alpha-L-iduronidase: characterization of the purified enzyme and correction of mucopolysaccharidosis type I fibroblasts.
    Unger EG; Durrant J; Anson DS; Hopwood JJ
    Biochem J; 1994 Nov; 304 ( Pt 1)(Pt 1):43-9. PubMed ID: 7998955
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Mobilization and transduction of peripheral blood progenitor cells in patients with mucopolysaccharidosis I.
    Hubel A; Stroncek D; Pan D; Whitley CB; McCullough J
    J Hematother; 1998 Dec; 7(6):505-14. PubMed ID: 9919944
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 8.