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6. Long-term correction of hyperphenylalaninemia by AAV-mediated gene transfer leads to behavioral recovery in phenylketonuria mice. Mochizuki S; Mizukami H; Ogura T; Kure S; Ichinohe A; Kojima K; Matsubara Y; Kobayahi E; Okada T; Hoshika A; Ozawa K; Kume A Gene Ther; 2004 Jul; 11(13):1081-6. PubMed ID: 15057263 [TBL] [Abstract][Full Text] [Related]
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13. Somatic gene therapy for phenylketonuria and other hepatic deficiencies. Eisensmith RC; Woo SL J Inherit Metab Dis; 1996; 19(4):412-23. PubMed ID: 8884565 [TBL] [Abstract][Full Text] [Related]
14. Reversal of metabolic and neurological symptoms of phenylketonuric mice treated with a PAH containing helper-dependent adenoviral vector. Cerreto M; Mehdawy B; Ombrone D; Nisticò R; Ruoppolo M; Usiello A; Daniele A; Pastore L; Salvatore F Curr Gene Ther; 2012 Feb; 12(1):48-56. PubMed ID: 22348550 [TBL] [Abstract][Full Text] [Related]
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19. Retroviral-mediated gene transfer of human phenylalanine hydroxylase into NIH 3T3 and hepatoma cells. Ledley FD; Grenett HE; McGinnis-Shelnutt M; Woo SL Proc Natl Acad Sci U S A; 1986 Jan; 83(2):409-13. PubMed ID: 3455778 [TBL] [Abstract][Full Text] [Related]