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14. Gene therapy progress and prospects: gene therapy of lysosomal storage disorders. Cheng SH; Smith AE Gene Ther; 2003 Aug; 10(16):1275-81. PubMed ID: 12883523 [TBL] [Abstract][Full Text] [Related]
15. Eighth International Symposium on Lysosomal Storage Diseases. Mehta AB; Germain DP; Martin R Int J Clin Pharmacol Ther; 2009; 47 Suppl 1():S1-3. PubMed ID: 20040305 [No Abstract] [Full Text] [Related]
16. [Allogeneic bone marrow transplantation in the treatment of (lysosomal) storage diseases]. Maaswinkel-Mooij PD; Poorthuis BJ; Hoogerbrugge PM; Brouwer OF; Vossen JM Ned Tijdschr Geneeskd; 1998 Jan; 142(4):169-74. PubMed ID: 9557021 [TBL] [Abstract][Full Text] [Related]
17. Use of nonviral promoters in adenovirus-mediated gene therapy: reduction of lysosomal storage in the aspartylglucosaminuria mouse. Virta S; Rapola J; Jalanko A; Laine M J Gene Med; 2006 Jun; 8(6):699-706. PubMed ID: 16518877 [TBL] [Abstract][Full Text] [Related]
18. Adenovirus-mediated gene transfer results in decreased lysosomal storage in brain and total correction in liver of aspartylglucosaminuria (AGU) mouse. Peltola M; Kyttälä A; Heinonen O; Rapola J; Paunio T; Revah F; Peltonen L; Jalanko A Gene Ther; 1998 Oct; 5(10):1314-21. PubMed ID: 9930336 [TBL] [Abstract][Full Text] [Related]
19. Advances in the treatment of lysosomal storage disease. Wraith JE Dev Med Child Neurol; 2001 Sep; 43(9):639-46. PubMed ID: 11570635 [No Abstract] [Full Text] [Related]
20. Farber's disease without central nervous system involvement: bone-marrow transplantation provides a promising new approach. Ehlert K; Roth J; Frosch M; Fehse N; Zander N; Vormoor J Ann Rheum Dis; 2006 Dec; 65(12):1665-6. PubMed ID: 17105855 [No Abstract] [Full Text] [Related] [Next] [New Search]