These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

225 related articles for article (PubMed ID: 9109535)

  • 1. Glycosaminoglycan storage in cultured neonatal murine mucopolysaccharidosis type VII neuroglial cells and correction by beta-glucuronidase gene transfer.
    Taylor RM; Wolfe JH
    J Neurochem; 1997 May; 68(5):2079-85. PubMed ID: 9109535
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Accumulation of abnormal amounts of glycosaminoglycans in murine mucopolysaccharidosis type VII neural progenitor cells does not alter the growth rate or efficiency of differentiation into neurons.
    Heuer GG; Skorupa AF; Prasad Alur RK; Jiang K; Wolfe JH
    Mol Cell Neurosci; 2001 Jan; 17(1):167-78. PubMed ID: 11161477
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Murine mucopolysaccharidosis type VII: the impact of therapies on the clinical course and pathology in a murine model of lysosomal storage disease.
    Vogler C; Sands MS; Galvin N; Levy B; Thorpe C; Barker J; Sly WS
    J Inherit Metab Dis; 1998 Aug; 21(5):575-86. PubMed ID: 9728337
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase.
    Taylor RM; Wolfe JH
    Nat Med; 1997 Jul; 3(7):771-4. PubMed ID: 9212105
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Comparison of ventricular and intravenous lentiviral-mediated gene therapy for murine MPS VII.
    Bielicki J; McIntyre C; Anson DS
    Mol Genet Metab; 2010 Dec; 101(4):370-82. PubMed ID: 20864369
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Lentiviral-mediated gene therapy results in sustained expression of β-glucuronidase for up to 12 months in the gus(mps/mps) and up to 18 months in the gus(tm(L175F)Sly) mouse models of mucopolysaccharidosis type VII.
    Derrick-Roberts AL; Pyragius CE; Kaidonis XM; Jackson MR; Anson DS; Byers S
    Hum Gene Ther; 2014 Sep; 25(9):798-810. PubMed ID: 25003807
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Widespread correction of lysosomal storage following intrahepatic injection of a recombinant adeno-associated virus in the adult MPS VII mouse.
    Sferra TJ; Backstrom K; Wang C; Rennard R; Miller M; Hu Y
    Mol Ther; 2004 Sep; 10(3):478-91. PubMed ID: 15336648
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Retroviral cDNA transfer to the RPE: stable expression and modification of metabolism.
    Ray J; Wolfe JH; Aguirre GD; Haskins ME
    Invest Ophthalmol Vis Sci; 1998 Aug; 39(9):1658-66. PubMed ID: 9699555
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Restoration of normal lysosomal function in mucopolysaccharidosis type VII cells by retroviral vector-mediated gene transfer.
    Wolfe JH; Schuchman EH; Stramm LE; Concaugh EA; Haskins ME; Aguirre GD; Patterson DF; Desnick RJ; Gilboa E
    Proc Natl Acad Sci U S A; 1990 Apr; 87(8):2877-81. PubMed ID: 2158095
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Clinical response to persistent, low-level beta-glucuronidase expression in the murine model of mucopolysaccharidosis type VII.
    Donsante A; Levy B; Vogler C; Sands MS
    J Inherit Metab Dis; 2007 Apr; 30(2):227-38. PubMed ID: 17308887
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse.
    Sferra TJ; Qu G; McNeely D; Rennard R; Clark KR; Lo WD; Johnson PR
    Hum Gene Ther; 2000 Mar; 11(4):507-19. PubMed ID: 10724030
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Evaluation of pathological manifestations of disease in mucopolysaccharidosis VII mice after neonatal hepatic gene therapy.
    Xu L; Mango RL; Sands MS; Haskins ME; Ellinwood NM; Ponder KP
    Mol Ther; 2002 Dec; 6(6):745-58. PubMed ID: 12498771
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Missense models [Gustm(E536A)Sly, Gustm(E536Q)Sly, and Gustm(L175F)Sly] of murine mucopolysaccharidosis type VII produced by targeted mutagenesis.
    Tomatsu S; Orii KO; Vogler C; Grubb JH; Snella EM; Gutierrez MA; Dieter T; Sukegawa K; Orii T; Kondo N; Sly WS
    Proc Natl Acad Sci U S A; 2002 Nov; 99(23):14982-7. PubMed ID: 12403825
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Single cell analysis and selection of living retrovirus vector-corrected mucopolysaccharidosis VII cells using a fluorescence-activated cell sorting-based assay for mammalian beta-glucuronidase enzymatic activity.
    Lorincz MC; Parente MK; Roederer M; Nolan GP; Diwu Z; Martin DI; Herzenberg LA; Wolfe JH
    J Biol Chem; 1999 Jan; 274(2):657-65. PubMed ID: 9872999
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.
    Daly TM; Okuyama T; Vogler C; Haskins ME; Muzyczka N; Sands MS
    Hum Gene Ther; 1999 Jan; 10(1):85-94. PubMed ID: 10022533
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Correction of murine mucopolysaccharidosis VII by a human beta-glucuronidase transgene.
    Kyle JW; Birkenmeier EH; Gwynn B; Vogler C; Hoppe PC; Hoffmann JW; Sly WS
    Proc Natl Acad Sci U S A; 1990 May; 87(10):3914-8. PubMed ID: 2111021
    [TBL] [Abstract][Full Text] [Related]  

  • 17. AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice.
    Hennig AK; Ogilvie JM; Ohlemiller KK; Timmers AM; Hauswirth WW; Sands MS
    Mol Ther; 2004 Jul; 10(1):106-16. PubMed ID: 15233947
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Early onset of lysosomal storage disease in a murine model of mucopolysaccharidosis type VII: undegraded substrate accumulates in many tissues in the fetus and very young MPS VII mouse.
    Vogler C; Levy B; Galvin N; Lessard M; Soper B; Barker J
    Pediatr Dev Pathol; 2005; 8(4):453-62. PubMed ID: 16222480
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Production of MPS VII mouse (Gus(tm(hE540A x mE536A)Sly)) doubly tolerant to human and mouse beta-glucuronidase.
    Tomatsu S; Orii KO; Vogler C; Grubb JH; Snella EM; Gutierrez M; Dieter T; Holden CC; Sukegawa K; Orii T; Kondo N; Sly WS
    Hum Mol Genet; 2003 May; 12(9):961-73. PubMed ID: 12700165
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Enzyme replacement in murine mucopolysaccharidosis type VII: neuronal and glial response to beta-glucuronidase requires early initiation of enzyme replacement therapy.
    Vogler C; Levy B; Galvin NJ; Thorpe C; Sands MS; Barker JE; Baty J; Birkenmeier EH; Sly WS
    Pediatr Res; 1999 Jun; 45(6):838-44. PubMed ID: 10367775
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 12.