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2. Gene transfer as an approach to treating hemophilia. High KA Semin Thromb Hemost; 2003 Feb; 29(1):107-20. PubMed ID: 12640573 [TBL] [Abstract][Full Text] [Related]
3. Muscle-directed gene transfer and transient immune suppression result in sustained partial correction of canine hemophilia B caused by a null mutation. Herzog RW; Mount JD; Arruda VR; High KA; Lothrop CD Mol Ther; 2001 Sep; 4(3):192-200. PubMed ID: 11545609 [TBL] [Abstract][Full Text] [Related]
4. Gene therapy for hemophilia: clinical trials and technical tribulations. Viiala NO; Larsen SR; Rasko JE Semin Thromb Hemost; 2009 Feb; 35(1):81-92. PubMed ID: 19308896 [TBL] [Abstract][Full Text] [Related]
5. AAV-mediated gene transfer for the treatment of hemophilia B: problems and prospects. Hasbrouck NC; High KA Gene Ther; 2008 Jun; 15(11):870-5. PubMed ID: 18432276 [TBL] [Abstract][Full Text] [Related]
6. Theodore E. Woodward Award. AAV-mediated gene transfer for hemophilia. High KA Trans Am Clin Climatol Assoc; 2003; 114():337-51; discussion 351-2. PubMed ID: 12813929 [TBL] [Abstract][Full Text] [Related]
7. AAV vectors for hemophilia B gene therapy. Chao H; Walsh CE Mt Sinai J Med; 2004 Oct; 71(5):305-13. PubMed ID: 15543431 [TBL] [Abstract][Full Text] [Related]
8. Implantation of autologous skin fibroblast genetically modified to secrete clotting factor IX partially corrects the hemorrhagic tendencies in two hemophilia B patients. Qiu X; Lu D; Zhou J; Wang J; Yang J; Meng P; Hsueh JL Chin Med J (Engl); 1996 Nov; 109(11):832-9. PubMed ID: 9275366 [TBL] [Abstract][Full Text] [Related]
9. Towards gene therapy for haemophilia B using primary human keratinocytes. Gerrard AJ; Hudson DL; Brownlee GG; Watt FM Nat Genet; 1993 Feb; 3(2):180-3. PubMed ID: 8499952 [TBL] [Abstract][Full Text] [Related]
10. Therapeutic plasma concentrations of human factor IX in mice after gene delivery into the amniotic cavity: a model for the prenatal treatment of haemophilia B. Schneider H; Adebakin S; Themis M; Cook T; Douar AM; Pavirani A; Coutelle C J Gene Med; 1999; 1(6):424-32. PubMed ID: 10753068 [TBL] [Abstract][Full Text] [Related]
11. Risk and prevention of anti-factor IX formation in AAV-mediated gene transfer in the context of a large deletion of F9. Fields PA; Arruda VR; Armstrong E; Chu K; Mingozzi F; Hagstrom JN; Herzog RW; High KA Mol Ther; 2001 Sep; 4(3):201-10. PubMed ID: 11545610 [TBL] [Abstract][Full Text] [Related]
12. Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors. Snyder RO; Miao C; Meuse L; Tubb J; Donahue BA; Lin HF; Stafford DW; Patel S; Thompson AR; Nichols T; Read MS; Bellinger DA; Brinkhous KM; Kay MA Nat Med; 1999 Jan; 5(1):64-70. PubMed ID: 9883841 [TBL] [Abstract][Full Text] [Related]
13. Towards gene therapy for hemophilia B. Anson DS; Hock RA; Austen D; Smith KJ; Brownlee GG; Verma IM; Miller AD Mol Biol Med; 1987 Feb; 4(1):11-20. PubMed ID: 3475525 [TBL] [Abstract][Full Text] [Related]
14. Gene therapy for haemophilia B. Tuddenham E Haemophilia; 2012 Jul; 18 Suppl 4():13-7. PubMed ID: 22726076 [TBL] [Abstract][Full Text] [Related]
15. Adeno-associated virus-mediated gene transfer of factor IX for treatment of hemophilia B by gene therapy. Herzog RW; High KA Thromb Haemost; 1999 Aug; 82(2):540-6. PubMed ID: 10605748 [No Abstract] [Full Text] [Related]
16. Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors. Snyder RO; Miao CH; Patijn GA; Spratt SK; Danos O; Nagy D; Gown AM; Winther B; Meuse L; Cohen LK; Thompson AR; Kay MA Nat Genet; 1997 Jul; 16(3):270-6. PubMed ID: 9207793 [TBL] [Abstract][Full Text] [Related]
20. Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. Kay MA; Manno CS; Ragni MV; Larson PJ; Couto LB; McClelland A; Glader B; Chew AJ; Tai SJ; Herzog RW; Arruda V; Johnson F; Scallan C; Skarsgard E; Flake AW; High KA Nat Genet; 2000 Mar; 24(3):257-61. PubMed ID: 10700178 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]