208 related articles for article (PubMed ID: 9560205)
1. Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs.
Gorman L; Suter D; Emerick V; Schümperli D; Kole R
Proc Natl Acad Sci U S A; 1998 Apr; 95(9):4929-34. PubMed ID: 9560205
[TBL] [Abstract][Full Text] [Related]
2. Double-target antisense U7 snRNAs promote efficient skipping of an aberrant exon in three human beta-thalassemic mutations.
Suter D; Tomasini R; Reber U; Gorman L; Kole R; Schümperli D
Hum Mol Genet; 1999 Dec; 8(13):2415-23. PubMed ID: 10556289
[TBL] [Abstract][Full Text] [Related]
3. Restoration of correct splicing of thalassemic beta-globin pre-mRNA by modified U1 snRNAs.
Gorman L; Mercatante DR; Kole R
J Biol Chem; 2000 Nov; 275(46):35914-9. PubMed ID: 10969081
[TBL] [Abstract][Full Text] [Related]
4. Restoration of correct β
Nualkaew T; Jearawiriyapaisarn N; Hongeng S; Fucharoen S; Kole R; Svasti S
Sci Rep; 2019 May; 9(1):7672. PubMed ID: 31113996
[TBL] [Abstract][Full Text] [Related]
5. Engineered U7 snRNA mediates sustained splicing correction in erythroid cells from β-thalassemia/HbE patients.
Preedagasamzin S; Nualkaew T; Pongrujikorn T; Jinawath N; Kole R; Fucharoen S; Jearawiriyapaisarn N; Svasti S
Biochem Biophys Res Commun; 2018 Apr; 499(1):86-92. PubMed ID: 29550480
[TBL] [Abstract][Full Text] [Related]
6. Enhancement of β-Globin Gene Expression in Thalassemic IVS2-654 Induced Pluripotent Stem Cell-Derived Erythroid Cells by Modified U7 snRNA.
Phanthong P; Borwornpinyo S; Kitiyanant N; Jearawiriyapaisarn N; Nuntakarn L; Saetan J; Nualkaew T; Sa-Ngiamsuntorn K; Anurathapan U; Dinnyes A; Kitiyanant Y; Hongeng S
Stem Cells Transl Med; 2017 Apr; 6(4):1059-1069. PubMed ID: 28213976
[TBL] [Abstract][Full Text] [Related]
7. High-level expression of hemoglobin A in human thalassemic erythroid progenitor cells following lentiviral vector delivery of an antisense snRNA.
Vacek MM; Ma H; Gemignani F; Lacerra G; Kafri T; Kole R
Blood; 2003 Jan; 101(1):104-11. PubMed ID: 12393543
[TBL] [Abstract][Full Text] [Related]
8. Restoration of correct splicing in thalassemic pre-mRNA by antisense oligonucleotides.
Dominski Z; Kole R
Proc Natl Acad Sci U S A; 1993 Sep; 90(18):8673-7. PubMed ID: 8378346
[TBL] [Abstract][Full Text] [Related]
9. Repair of thalassemic human beta-globin mRNA in mammalian cells by antisense oligonucleotides.
Sierakowska H; Sambade MJ; Agrawal S; Kole R
Proc Natl Acad Sci U S A; 1996 Nov; 93(23):12840-4. PubMed ID: 8917506
[TBL] [Abstract][Full Text] [Related]
10. Engineered U7 Small Nuclear RNA Restores Correct β-Globin Pre-mRNA Splicing in Mouse β
d'Arqom A; Nualkaew T; Jearawiriyapaisarn N; Kole R; Svasti S
Hum Gene Ther; 2021 May; 32(9-10):473-480. PubMed ID: 32977730
[TBL] [Abstract][Full Text] [Related]
11. Temperature-dependent splicing of beta-globin pre-mRNA.
Gemignani F; Sazani P; Morcos P; Kole R
Nucleic Acids Res; 2002 Nov; 30(21):4592-8. PubMed ID: 12409448
[TBL] [Abstract][Full Text] [Related]
12. Repair of a splicing defect in erythroid cells from patients with beta-thalassemia/HbE disorder.
Suwanmanee T; Sierakowska H; Fucharoen S; Kole R
Mol Ther; 2002 Dec; 6(6):718-26. PubMed ID: 12498768
[TBL] [Abstract][Full Text] [Related]
13. U7 snRNA-mediated correction of aberrant splicing caused by activation of cryptic splice sites.
Uchikawa H; Fujii K; Kohno Y; Katsumata N; Nagao K; Yamada M; Miyashita T
J Hum Genet; 2007; 52(11):891-897. PubMed ID: 17851636
[TBL] [Abstract][Full Text] [Related]
14. Sensitivity of splice sites to antisense oligonucleotides in vivo.
Sierakowska H; Sambade MJ; Schümperli D; Kole R
RNA; 1999 Mar; 5(3):369-77. PubMed ID: 10094306
[TBL] [Abstract][Full Text] [Related]
15. Reversal of aberrant splicing of beta-thalassemia allele by antisense RNA in vitro and in vivo.
Zeng Y; Gu X; Chen Y; Gong L; Ren Z; Huang S
Chin Med J (Engl); 1999 Feb; 112(2):107-11. PubMed ID: 11593572
[TBL] [Abstract][Full Text] [Related]
16. [Repair of the splicing defect of thalassemic allele beta IVS-2-654 C-->T in cultured human erythroid cells by antisense RNA].
Gu X; Gong L; Zhang W
Zhonghua Yi Xue Za Zhi; 1997 Nov; 77(11):815-8. PubMed ID: 9772473
[TBL] [Abstract][Full Text] [Related]
17. Doxycycline-controlled splicing modulation by regulated antisense U7 snRNA expression cassettes.
Marquis J; Kämpfer SS; Angehrn L; Schümperli D
Gene Ther; 2009 Jan; 16(1):70-7. PubMed ID: 18701908
[TBL] [Abstract][Full Text] [Related]
18. A single-base change at a splice site in a beta 0-thalassemic gene causes abnormal RNA splicing.
Treisman R; Proudfoot NJ; Shander M; Maniatis T
Cell; 1982 Jul; 29(3):903-11. PubMed ID: 7151176
[TBL] [Abstract][Full Text] [Related]
19. Restoration of human beta-globin gene expression in murine and human IVS2-654 thalassemic erythroid cells by free uptake of antisense oligonucleotides.
Suwanmanee T; Sierakowska H; Lacerra G; Svasti S; Kirby S; Walsh CE; Fucharoen S; Kole R
Mol Pharmacol; 2002 Sep; 62(3):545-53. PubMed ID: 12181431
[TBL] [Abstract][Full Text] [Related]
20. Beta + thalassemia: aberrant splicing results from a single point mutation in an intron.
Busslinger M; Moschonas N; Flavell RA
Cell; 1981 Dec; 27(2 Pt 1):289-98. PubMed ID: 6895866
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
