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2. Drug development. Orphan drug windfalls? Gershon D Nature; 1992 Jan; 355(6359):381. PubMed ID: 1734267 [No Abstract] [Full Text] [Related]
3. Creating the costliest orphan. The Orphan Drug Act in the development of Ceredase. Goldman DP; Clarke AE; Garber AM Int J Technol Assess Health Care; 1992; 8(4):583-97. PubMed ID: 1464480 [TBL] [Abstract][Full Text] [Related]
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5. Current status of orphan disease drug development. Thoene JG Curr Opin Pediatr; 1994 Apr; 6(2):209-12. PubMed ID: 8032402 [TBL] [Abstract][Full Text] [Related]
6. Why Genzyme can charge so much for Cerezyme. Anand G Wall St J (East Ed); 2005 Nov; ():A15. PubMed ID: 16502533 [No Abstract] [Full Text] [Related]
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12. Approval times for supplemental indications for recombinant proteins. Gosse ME; Nelson TF Nat Biotechnol; 1997 Feb; 15(2):130-4. PubMed ID: 9035135 [No Abstract] [Full Text] [Related]
13. Rare diseases and orphan drugs. Daina E Lancet; 1994 Jun; 343(8912):1560-1. PubMed ID: 7911879 [No Abstract] [Full Text] [Related]
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17. Federal 340B Program Payment Scheme for Drugs Designated As Orphan Products: Congressional Clarification Needed to Close the Government-Industry Revolving Door. Yang YT; Chen B; Bennett CL J Clin Oncol; 2016 Dec; 34(36):4320-4322. PubMed ID: 27998222 [No Abstract] [Full Text] [Related]
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