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3. [Transplantation of genetically modified cells in the treatment of children with SCID: great hopes and recent disappointments]. Smogorzewska EM, Weinberg KI, Kohn DB. Med Wieku Rozwoj; 2003 Aug; 7(1):27-34. PubMed ID: 13130167 [Abstract] [Full Text] [Related]
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19. Amendment to Clinical Research Project. Project 90-C-195. April 1, 1993. Treatment of severe combined immunodeficiency disease (SCID) due to adenosine deaminase deficiency with autologous lymphocytes transduced with a human ADA gene. Dunbar C, Chang L, Mullen C, Ramsey WJ, Carter C, Kohn D, Parkman R, Lenarsky C, Weinberg K, Wara D, Culver KW, Anderson WF, Leitman S, Fleisher T, Klein H, Shearer G, Clerici M, McGarrity G, Bastian J, Hershfield MS. Hum Gene Ther; 1999 Feb 10; 10(3):477-88. PubMed ID: 10048399 [No Abstract] [Full Text] [Related]
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