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Journal Abstract Search
801 related items for PubMed ID: 15050976
1. Developing treatments for inborn errors: incentives available to the clinician. Haffner ME. Mol Genet Metab; 2004 Apr; 81 Suppl 1():S63-6. PubMed ID: 15050976 [Abstract] [Full Text] [Related]
2. Therapies for inborn errors of metabolism: what has the orphan drug act delivered? Talele SS, Xu K, Pariser AR, Braun MM, Farag-El-Massah S, Phillips MI, Thompson BH, Coté TR. Pediatrics; 2010 Jul; 126(1):101-6. PubMed ID: 20566615 [Abstract] [Full Text] [Related]
3. Drugs for rare diseases: mixed assessment in Europe. Prescrire Int; 2007 Feb; 16(87):36-42. PubMed ID: 17323539 [Abstract] [Full Text] [Related]
4. The US Orphan Drug Act: rare disease research stimulator or commercial opportunity? Wellman-Labadie O, Zhou Y. Health Policy; 2010 May; 95(2-3):216-28. PubMed ID: 20036435 [Abstract] [Full Text] [Related]
5. [Hope for patients with rare diseases--"orphan" drugs]. Kuzelová M, Kubácková K, Palágyi M, Smíd M. Cas Lek Cesk; 2006 May; 145(4):296-300. PubMed ID: 16639930 [Abstract] [Full Text] [Related]
6. A cross-national comparative study of orphan drug policies in the United States, the European Union, and Japan: towards a made-in-China orphan drug policy. Liu BC, He L, He G, He Y. J Public Health Policy; 2010 Dec; 31(4):407-20; discussion 420-1. PubMed ID: 21119648 [Abstract] [Full Text] [Related]
7. What the Orphan Drug Act has done lately for children with rare diseases: a 10-year analysis. Thorat C, Xu K, Freeman SN, Bonnel RA, Joseph F, Phillips MI, Imoisili MA. Pediatrics; 2012 Mar; 129(3):516-21. PubMed ID: 22371464 [Abstract] [Full Text] [Related]
8. Regulatory considerations for developing drugs for rare diseases: orphan designations and early phase clinical trials. Pariser AR, Xu K, Milto J, Coté TR. Discov Med; 2011 Apr; 11(59):367-75. PubMed ID: 21524390 [Abstract] [Full Text] [Related]
14. Orphan drug legislation: lessons for neglected tropical diseases. Villa S, Compagni A, Reich MR. Int J Health Plann Manage; 2009 May; 24(1):27-42. PubMed ID: 18435430 [Abstract] [Full Text] [Related]
15. Database identifies FDA-approved drugs with potential to be repurposed for treatment of orphan diseases. Xu K, Coté TR. Brief Bioinform; 2011 Jul; 12(4):341-5. PubMed ID: 21357612 [Abstract] [Full Text] [Related]
17. Incentivizing Orphan Product Development: United States Food and Drug Administration Orphan Incentive Programs. Le TT. Adv Exp Med Biol; 2017 Jul; 1031():183-196. PubMed ID: 29214572 [Abstract] [Full Text] [Related]