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2. Target selection for antisense oligonucleotide induced exon skipping in the dystrophin gene. Errington SJ, Mann CJ, Fletcher S, Wilton SD. J Gene Med; 2003 Jun; 5(6):518-27. PubMed ID: 12797117 [Abstract] [Full Text] [Related]
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4. Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD. McClorey G, Moulton HM, Iversen PL, Fletcher S, Wilton SD. Gene Ther; 2006 Oct; 13(19):1373-81. PubMed ID: 16724091 [Abstract] [Full Text] [Related]
10. Comparative analysis of antisense oligonucleotide analogs for targeted DMD exon 46 skipping in muscle cells. Aartsma-Rus A, Kaman WE, Bremmer-Bout M, Janson AA, den Dunnen JT, van Ommen GJ, van Deutekom JC. Gene Ther; 2004 Sep; 11(18):1391-8. PubMed ID: 15229633 [Abstract] [Full Text] [Related]
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12. Intraperitoneal administration of phosphorothioate antisense oligodeoxynucleotide against splicing enhancer sequence induced exon skipping in dystrophin mRNA expressed in mdx skeletal muscle. Takeshima Y, Yagi M, Wada H, Matsuo M. Brain Dev; 2005 Oct; 27(7):488-93. PubMed ID: 16198206 [Abstract] [Full Text] [Related]
15. DMD pseudoexon mutations: splicing efficiency, phenotype, and potential therapy. Gurvich OL, Tuohy TM, Howard MT, Finkel RS, Medne L, Anderson CB, Weiss RB, Wilton SD, Flanigan KM. Ann Neurol; 2008 Jan 02; 63(1):81-9. PubMed ID: 18059005 [Abstract] [Full Text] [Related]
16. Development of antisense-mediated exon skipping as a treatment for duchenne muscular dystrophy. Heemskerk H, de Winter CL, van Ommen GJ, van Deutekom JC, Aartsma-Rus A. Ann N Y Acad Sci; 2009 Sep 02; 1175():71-9. PubMed ID: 19796079 [Abstract] [Full Text] [Related]
17. Modification of pre-mRNA processing: application to dystrophin expression. Wilton SD, Fletcher S. Curr Opin Mol Ther; 2006 Apr 02; 8(2):130-5. PubMed ID: 16610765 [Abstract] [Full Text] [Related]