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2. Treatment of murine mucopolysaccharidosis type VII by syngeneic bone marrow transplantation in neonates. Sands MS, Barker JE, Vogler C, Levy B, Gwynn B, Galvin N, Sly WS, Birkenmeier E. Lab Invest; 1993 Jun; 68(6):676-86. PubMed ID: 8515654 [Abstract] [Full Text] [Related]
3. Bone marrow transplantation has a significant effect on enzyme levels and storage of glycosaminoglycans in tissues and in isolated hepatocytes of mucopolysaccharidosis type VII mice. Poorthuis BJ, Romme AE, Willemsen R, Wagemaker G. Pediatr Res; 1994 Aug; 36(2):187-93. PubMed ID: 7970933 [Abstract] [Full Text] [Related]
4. Correction of murine mucopolysaccharidosis VII by a human beta-glucuronidase transgene. Kyle JW, Birkenmeier EH, Gwynn B, Vogler C, Hoppe PC, Hoffmann JW, Sly WS. Proc Natl Acad Sci U S A; 1990 May; 87(10):3914-8. PubMed ID: 2111021 [Abstract] [Full Text] [Related]
5. Syngeneic bone marrow transplantation reduces the hearing loss associated with murine mucopolysaccharidosis type VII. Sands MS, Erway LC, Vogler C, Sly WS, Birkenmeier EH. Blood; 1995 Sep 01; 86(5):2033-40. PubMed ID: 7655032 [Abstract] [Full Text] [Related]
6. Murine mucopolysaccharidosis type VII: the impact of therapies on the clinical course and pathology in a murine model of lysosomal storage disease. Vogler C, Sands MS, Galvin N, Levy B, Thorpe C, Barker J, Sly WS. J Inherit Metab Dis; 1998 Aug 01; 21(5):575-86. PubMed ID: 9728337 [Abstract] [Full Text] [Related]
10. Disappearance of lysosomal storage in spleen and liver of mucopolysaccharidosis VII mice after transplantation of genetically modified bone marrow cells. Maréchal V, Naffakh N, Danos O, Heard JM. Blood; 1993 Aug 15; 82(4):1358-65. PubMed ID: 8353294 [Abstract] [Full Text] [Related]
12. Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency. Birkenmeier EH, Davisson MT, Beamer WG, Ganschow RE, Vogler CA, Gwynn B, Lyford KA, Maltais LM, Wawrzyniak CJ. J Clin Invest; 1989 Apr 15; 83(4):1258-66. PubMed ID: 2495302 [Abstract] [Full Text] [Related]
13. A murine model of mucopolysaccharidosis VII. Gross and microscopic findings in beta-glucuronidase-deficient mice. Vogler C, Birkenmeier EH, Sly WS, Levy B, Pegors C, Kyle JW, Beamer WG. Am J Pathol; 1990 Jan 15; 136(1):207-17. PubMed ID: 2105058 [Abstract] [Full Text] [Related]
14. Glycosaminoglycan storage in cultured neonatal murine mucopolysaccharidosis type VII neuroglial cells and correction by beta-glucuronidase gene transfer. Taylor RM, Wolfe JH. J Neurochem; 1997 May 15; 68(5):2079-85. PubMed ID: 9109535 [Abstract] [Full Text] [Related]
15. Vestronidase alfa: Recombinant human β-glucuronidase as an enzyme replacement therapy for MPS VII. Cadaoas J, Boyle G, Jungles S, Cullen S, Vellard M, Grubb JH, Jurecka A, Sly W, Kakkis E. Mol Genet Metab; 2020 May 15; 130(1):65-76. PubMed ID: 32192868 [Abstract] [Full Text] [Related]
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17. Widespread biochemical correction of murine mucopolysaccharidosis type VII pathology by liver hydrodynamic plasmid delivery. Richard M, Arfi A, Seguin J, Gandolphe C, Scherman D. Gene Ther; 2009 Jun 01; 16(6):746-56. PubMed ID: 19357715 [Abstract] [Full Text] [Related]
18. Behavioral consequences of bone marrow transplantation in the treatment of murine mucopolysaccharidosis type VII. Bastedo L, Sands MS, Lambert DT, Pisa MA, Birkenmeier E, Chang PL. J Clin Invest; 1994 Sep 01; 94(3):1180-6. PubMed ID: 8083358 [Abstract] [Full Text] [Related]
19. Enzyme replacement in murine mucopolysaccharidosis type VII: neuronal and glial response to beta-glucuronidase requires early initiation of enzyme replacement therapy. Vogler C, Levy B, Galvin NJ, Thorpe C, Sands MS, Barker JE, Baty J, Birkenmeier EH, Sly WS. Pediatr Res; 1999 Jun 01; 45(6):838-44. PubMed ID: 10367775 [Abstract] [Full Text] [Related]
20. Murine mucopolysaccharidosis type VII: long term therapeutic effects of enzyme replacement and enzyme replacement followed by bone marrow transplantation. Sands MS, Vogler C, Torrey A, Levy B, Gwynn B, Grubb J, Sly WS, Birkenmeier EH. J Clin Invest; 1997 Apr 01; 99(7):1596-605. PubMed ID: 9120003 [Abstract] [Full Text] [Related] Page: [Next] [New Search]