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7. Genomic Variability in the Survival Motor Neuron Genes (SMN1 and SMN2): Implications for Spinal Muscular Atrophy Phenotype and Therapeutics Development. Butchbach MER. Int J Mol Sci; 2021 Jul 23; 22(15):. PubMed ID: 34360669 [Abstract] [Full Text] [Related]
8. Delivery of bifunctional RNAs that target an intronic repressor and increase SMN levels in an animal model of spinal muscular atrophy. Baughan TD, Dickson A, Osman EY, Lorson CL. Hum Mol Genet; 2009 May 01; 18(9):1600-11. PubMed ID: 19228773 [Abstract] [Full Text] [Related]
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