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Journal Abstract Search
799 related items for PubMed ID: 23165354
1. New strategies for the treatment of lysosomal storage diseases (review). Parenti G, Pignata C, Vajro P, Salerno M. Int J Mol Med; 2013 Jan; 31(1):11-20. PubMed ID: 23165354 [Abstract] [Full Text] [Related]
3. Lysosomal storage diseases: from pathophysiology to therapy. Parenti G, Andria G, Ballabio A. Annu Rev Med; 2015 Dec; 66():471-86. PubMed ID: 25587658 [Abstract] [Full Text] [Related]
4. Treatment options for lysosomal storage disorders: developing insights. van Gelder CM, Vollebregt AA, Plug I, van der Ploeg AT, Reuser AJ. Expert Opin Pharmacother; 2012 Nov; 13(16):2281-99. PubMed ID: 23009070 [Abstract] [Full Text] [Related]
6. Recent developments in therapeutic approaches for lysosomal storage diseases. Urbanelli L, Magini A, Polchi A, Polidoro M, Emiliani C. Recent Pat CNS Drug Discov; 2011 Jan; 6(1):1-19. PubMed ID: 21073432 [Abstract] [Full Text] [Related]
7. Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications. Biffi A. Mol Ther; 2017 May 03; 25(5):1155-1162. PubMed ID: 28389320 [Abstract] [Full Text] [Related]
8. Gene therapy for the lysosomal storage disorders. Cabrera-Salazar MA, Novelli E, Barranger JA. Curr Opin Mol Ther; 2002 Aug 03; 4(4):349-58. PubMed ID: 12222873 [Abstract] [Full Text] [Related]
9. Current state of the management of LSDs. Germain DP, Aggio M. Int J Clin Pharmacol Ther; 2009 Aug 03; 47 Suppl 1():S61-2. PubMed ID: 20040313 [No Abstract] [Full Text] [Related]
10. Current strategies in the management of lysosomal storage diseases. Heese BA. Semin Pediatr Neurol; 2008 Sep 03; 15(3):119-26. PubMed ID: 18708002 [Abstract] [Full Text] [Related]
11. Neurological manifestations in lysosomal storage disorders - from pathology to first therapeutic possibilities. Hoffmann B, Mayatepek E. Neuropediatrics; 2005 Oct 03; 36(5):285-9. PubMed ID: 16217702 [Abstract] [Full Text] [Related]
12. [Therapy of lysosomal storage diseases: update and perspectives]. Lara-Aguilar RA, Juárez-Vázquez CI, Medina-Lozano C. Rev Invest Clin; 2011 Oct 03; 63(6):651-8. PubMed ID: 23650678 [Abstract] [Full Text] [Related]
13. Newborn screening for lysosomal storage disorders. Nakamura K, Hattori K, Endo F. Am J Med Genet C Semin Med Genet; 2011 Feb 15; 157C(1):63-71. PubMed ID: 21312327 [Abstract] [Full Text] [Related]
14. Treatment strategies for lysosomal storage disorders. Beck M. Dev Med Child Neurol; 2018 Jan 15; 60(1):13-18. PubMed ID: 29090451 [Abstract] [Full Text] [Related]
15. Combination Therapies for Lysosomal Storage Diseases: A Complex Answer to a Simple Problem. Macauley SL. Pediatr Endocrinol Rev; 2016 Jun 15; 13 Suppl 1(Suppl 1):639-48. PubMed ID: 27491211 [Abstract] [Full Text] [Related]
16. Personalized Pharmacoperones for Lysosomal Storage Disorder: Approach for Next-Generation Treatment. Haneef SA, Doss CG. Adv Protein Chem Struct Biol; 2016 Jun 15; 102():225-65. PubMed ID: 26827607 [Abstract] [Full Text] [Related]
17. Lysosomal storage disorders: old diseases, present and future challenges. Klein AD, Futerman AH. Pediatr Endocrinol Rev; 2013 Nov 15; 11 Suppl 1():59-63. PubMed ID: 24380123 [Abstract] [Full Text] [Related]
18. Oral small molecule therapy for lysosomal storage diseases. Weinreb NJ. Pediatr Endocrinol Rev; 2013 Nov 15; 11 Suppl 1():77-90. PubMed ID: 24380126 [Abstract] [Full Text] [Related]
19. Therapy for lysosomal storage disorders. Beck M. IUBMB Life; 2010 Jan 15; 62(1):33-40. PubMed ID: 20014233 [Abstract] [Full Text] [Related]