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4. Improved efficacy of a next-generation ERT in murine Pompe disease. Xu S, Lun Y, Frascella M, Garcia A, Soska R, Nair A, Ponery AS, Schilling A, Feng J, Tuske S, Valle MCD, Martina JA, Ralston E, Gotschall R, Valenzano KJ, Puertollano R, Do HV, Raben N, Khanna R. JCI Insight; 2019 Mar 07; 4(5):. PubMed ID: 30843882 [Abstract] [Full Text] [Related]
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