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PUBMED FOR HANDHELDS

Journal Abstract Search


373 related items for PubMed ID: 31402115

  • 1.
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  • 2. Generation of induced pluripotent stem cells-derived hepatocyte-like cells for ex vivo gene therapy of primary hyperoxaluria type 1.
    Estève J, Blouin JM, Lalanne M, Azzi-Martin L, Dubus P, Bidet A, Harambat J, Llanas B, Moranvillier I, Bedel A, Moreau-Gaudry F, Richard E.
    Stem Cell Res; 2019 Jul; 38():101467. PubMed ID: 31151050
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  • 4. Generation of a Primary Hyperoxaluria Type 1 Disease Model Via CRISPR/Cas9 System in Rats.
    Zheng R, Fang X, He L, Shao Y, Guo N, Wang L, Liu M, Li D, Geng H.
    Curr Mol Med; 2018 Jul; 18(7):436-447. PubMed ID: 30539697
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  • 5. CRISPR/Cas9-mediated glycolate oxidase disruption is an efficacious and safe treatment for primary hyperoxaluria type I.
    Zabaleta N, Barberia M, Martin-Higueras C, Zapata-Linares N, Betancor I, Rodriguez S, Martinez-Turrillas R, Torella L, Vales A, Olagüe C, Vilas-Zornoza A, Castro-Labrador L, Lara-Astiaso D, Prosper F, Salido E, Gonzalez-Aseguinolaza G, Rodriguez-Madoz JR.
    Nat Commun; 2018 Dec 21; 9(1):5454. PubMed ID: 30575740
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  • 6. Generation and characterization of a novel rat model of primary hyperoxaluria type 1 with a nonsense mutation in alanine-glyoxylate aminotransferase gene.
    Li Y, Zheng R, Xu G, Huang Y, Li Y, Li D, Geng H.
    Am J Physiol Renal Physiol; 2021 Mar 01; 320(3):F475-F484. PubMed ID: 33491567
    [Abstract] [Full Text] [Related]

  • 7. Differential Transgene Silencing of Myeloid-Specific Promoters in the AAVS1 Safe Harbor Locus of Induced Pluripotent Stem Cell-Derived Myeloid Cells.
    Klatt D, Cheng E, Hoffmann D, Santilli G, Thrasher AJ, Brendel C, Schambach A.
    Hum Gene Ther; 2020 Feb 01; 31(3-4):199-210. PubMed ID: 31773990
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  • 8. Correction of hyperoxaluria by liver repopulation with hepatocytes in a mouse model of primary hyperoxaluria type-1.
    Jiang J, Salido EC, Guha C, Wang X, Moitra R, Liu L, Roy-Chowdhury J, Roy-Chowdhury N.
    Transplantation; 2008 May 15; 85(9):1253-60. PubMed ID: 18475180
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  • 10. CRISPR/Cas9-mediated metabolic pathway reprogramming in a novel humanized rat model ameliorates primary hyperoxaluria type 1.
    Zheng R, Li Y, Wang L, Fang X, Zhang J, He L, Yang L, Li D, Geng H.
    Kidney Int; 2020 Oct 15; 98(4):947-957. PubMed ID: 32464217
    [Abstract] [Full Text] [Related]

  • 11. CRISPR/Cas9-mediated gene correction in hemophilia B patient-derived iPSCs.
    Morishige S, Mizuno S, Ozawa H, Nakamura T, Mazahery A, Nomura K, Seki R, Mouri F, Osaki K, Yamamura K, Okamura T, Nagafuji K.
    Int J Hematol; 2020 Feb 15; 111(2):225-233. PubMed ID: 31664646
    [Abstract] [Full Text] [Related]

  • 12. Systemic Alanine Glyoxylate Aminotransferase mRNA Improves Glyoxylate Metabolism in a Mouse Model of Primary Hyperoxaluria Type 1.
    Kukreja A, Lasaro M, Cobaugh C, Forbes C, Tang JP, Gao X, Martin-Higueras C, Pey AL, Salido E, Sobolov S, Subramanian RR.
    Nucleic Acid Ther; 2019 Apr 15; 29(2):104-113. PubMed ID: 30676254
    [Abstract] [Full Text] [Related]

  • 13. Generation of an induced pluripotent stem cell line (CIMAi001-A) from a compound heterozygous Primary Hyperoxaluria Type I (PH1) patient carrying p.G170R and p.R122* mutations in the AGXT gene.
    Martinez-Turrillas R, Rodriguez-Diaz S, Rodriguez-Marquez P, Martin-Mallo A, Salido E, Beck BB, Prosper F, Rodriguez-Madoz JR.
    Stem Cell Res; 2019 Dec 15; 41():101626. PubMed ID: 31715429
    [Abstract] [Full Text] [Related]

  • 14. In vivo base editing rescues primary hyperoxaluria type 1 in rats.
    Chen Z, Zhang D, Zheng R, Yang L, Huo Y, Zhang D, Fang X, Li Y, Xu G, Li D, Geng H.
    Kidney Int; 2024 Mar 15; 105(3):496-507. PubMed ID: 38142039
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  • 15. Restored glyoxylate metabolism after AGXT gene correction and direct reprogramming of primary hyperoxaluria type 1 fibroblasts.
    Nieto-Romero V, García-Torralba A, Molinos-Vicente A, Moya FJ, Rodríguez-Perales S, García-Escudero R, Salido E, Segovia JC, García-Bravo M.
    iScience; 2024 Apr 19; 27(4):109530. PubMed ID: 38577102
    [Abstract] [Full Text] [Related]

  • 16. Helper-dependent adenoviral vectors for liver-directed gene therapy of primary hyperoxaluria type 1.
    Castello R, Borzone R, D'Aria S, Annunziata P, Piccolo P, Brunetti-Pierri N.
    Gene Ther; 2016 Feb 19; 23(2):129-34. PubMed ID: 26609667
    [Abstract] [Full Text] [Related]

  • 17. Phenotypic correction of a mouse model for primary hyperoxaluria with adeno-associated virus gene transfer.
    Salido E, Rodriguez-Pena M, Santana A, Beattie SG, Petry H, Torres A.
    Mol Ther; 2011 May 19; 19(5):870-5. PubMed ID: 21119625
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  • 18. CRISPR-Cas9-Based Genome Editing of Human Induced Pluripotent Stem Cells.
    Giacalone JC, Sharma TP, Burnight ER, Fingert JF, Mullins RF, Stone EM, Tucker BA.
    Curr Protoc Stem Cell Biol; 2018 Feb 28; 44():5B.7.1-5B.7.22. PubMed ID: 29512106
    [Abstract] [Full Text] [Related]

  • 19. Multiplex gene editing reduces oxalate production in primary hyperoxaluria type 1.
    Zheng R, Zhang DX, Shao YJ, Fang XL, Yang L, Huo YN, Li DL, Geng HQ.
    Zool Res; 2023 Nov 18; 44(6):993-1002. PubMed ID: 37759334
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  • 20. Curative Ex Vivo Hepatocyte-Directed Gene Editing in a Mouse Model of Hereditary Tyrosinemia Type 1.
    VanLith C, Guthman R, Nicolas CT, Allen K, Du Z, Joo DJ, Nyberg SL, Lillegard JB, Hickey RD.
    Hum Gene Ther; 2018 Nov 18; 29(11):1315-1326. PubMed ID: 29764210
    [Abstract] [Full Text] [Related]


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