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4. Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency. Garcia-Gomez M, Calabria A, Garcia-Bravo M, Benedicenti F, Kosinski P, López-Manzaneda S, Hill C, Del Mar Mañu-Pereira M, Martín MA, Orman I, Vives-Corrons JL, Kung C, Schambach A, Jin S, Bueren JA, Montini E, Navarro S, Segovia JC. Mol Ther; 2016 Aug; 24(7):1187-98. PubMed ID: 27138040 [Abstract] [Full Text] [Related]
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