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4. Agalsidase alfa in pediatric patients with Fabry disease: a 6.5-year open-label follow-up study. Schiffmann R, Pastores GM, Lien YH, Castaneda V, Chang P, Martin R, Wijatyk A. Orphanet J Rare Dis; 2014 Nov 26; 9():169. PubMed ID: 25425121 [Abstract] [Full Text] [Related]
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