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PUBMED FOR HANDHELDS

Journal Abstract Search


134 related items for PubMed ID: 38294974

  • 21. Voxelotor in adolescents and adults with sickle cell disease (HOPE): long-term follow-up results of an international, randomised, double-blind, placebo-controlled, phase 3 trial.
    Howard J, Ataga KI, Brown RC, Achebe M, Nduba V, El-Beshlawy A, Hassab H, Agodoa I, Tonda M, Gray S, Lehrer-Graiwer J, Vichinsky E.
    Lancet Haematol; 2021 May; 8(5):e323-e333. PubMed ID: 33838113
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  • 22. Efficacy of miglustat in Niemann-Pick C disease: a single centre experience.
    Ginocchio VM, D'Amico A, Bertini E, Ceravolo F, Dardis A, Verrigni D, Bembi B, Dionisi-Vici C, Deodato F.
    Mol Genet Metab; 2013 Nov; 110(3):329-35. PubMed ID: 23973268
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  • 25. Eltrombopag for children with chronic immune thrombocytopenia (PETIT2): a randomised, multicentre, placebo-controlled trial.
    Grainger JD, Locatelli F, Chotsampancharoen T, Donyush E, Pongtanakul B, Komvilaisak P, Sosothikul D, Drelichman G, Sirachainan N, Holzhauer S, Lebedev V, Lemons R, Pospisilova D, Ramenghi U, Bussel JB, Bakshi KK, Iyengar M, Chan GW, Chagin KD, Theodore D, Marcello LM, Bailey CK.
    Lancet; 2015 Oct 24; 386(10004):1649-58. PubMed ID: 26231455
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  • 28. Disease characteristics, prognosis and miglustat treatment effects on disease progression in patients with Niemann-Pick disease Type C: an international, multicenter, retrospective chart review.
    Pineda M, Juríčková K, Karimzadeh P, Kolnikova M, Malinova V, Insua JL, Velten C, Kolb SA.
    Orphanet J Rare Dis; 2019 Jan 08; 14(1):32. PubMed ID: 30732631
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  • 29. Safety and efficacy of pitolisant in children aged 6 years or older with narcolepsy with or without cataplexy: a double-blind, randomised, placebo-controlled trial.
    Dauvilliers Y, Lecendreux M, Lammers GJ, Franco P, Poluektov M, Caussé C, Lecomte I, Lecomte JM, Lehert P, Schwartz JC, Plazzi G.
    Lancet Neurol; 2023 Apr 08; 22(4):303-311. PubMed ID: 36931805
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  • 31. Identifying Niemann-Pick type C in early-onset ataxia: two quick clinical screening tools.
    Synofzik M, Fleszar Z, Schöls L, Just J, Bauer P, Torres Martin JV, Kolb S.
    J Neurol; 2016 Oct 08; 263(10):1911-8. PubMed ID: 27314965
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  • 32. Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study.
    Patterson MC, Vecchio D, Prady H, Abel L, Wraith JE.
    Lancet Neurol; 2007 Sep 08; 6(9):765-72. PubMed ID: 17689147
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  • 34. Visceral symptoms as a key diagnostic sign for the early infantile form of Niemann-Pick disease type C in a Russian patient: a case report.
    Degtyareva AV, Mikhailova SV, Zakharova EY, Tumanova EL, Puchkova AA.
    J Med Case Rep; 2016 Jun 01; 10(1):143. PubMed ID: 27250337
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  • 36. Long-term follow-up from the ORATORIO trial of ocrelizumab for primary progressive multiple sclerosis: a post-hoc analysis from the ongoing open-label extension of the randomised, placebo-controlled, phase 3 trial.
    Wolinsky JS, Arnold DL, Brochet B, Hartung HP, Montalban X, Naismith RT, Manfrini M, Overell J, Koendgen H, Sauter A, Bennett I, Hubeaux S, Kappos L, Hauser SL.
    Lancet Neurol; 2020 Dec 01; 19(12):998-1009. PubMed ID: 33129442
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  • 38. Double-Blind, Randomized, Placebo-Controlled Phase III Clinical Trial to Evaluate the Efficacy and Safety of treating Healthcare Professionals with the Adsorbed COVID-19 (Inactivated) Vaccine Manufactured by Sinovac - PROFISCOV: A structured summary of a study protocol for a randomised controlled trial.
    Palacios R, Patiño EG, de Oliveira Piorelli R, Conde MTRP, Batista AP, Zeng G, Xin Q, Kallas EG, Flores J, Ockenhouse CF, Gast C.
    Trials; 2020 Oct 15; 21(1):853. PubMed ID: 33059771
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  • 39. A randomized, double-blind, placebo-controlled phase III clinical trial to evaluate the efficacy and safety of SARS-CoV-2 vaccine (inactivated, Vero cell): a structured summary of a study protocol for a randomised controlled trial.
    Akova M, Unal S.
    Trials; 2021 Apr 13; 22(1):276. PubMed ID: 33849629
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