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8. [Transplantation of genetically modified cells in the treatment of children with SCID: great hopes and recent disappointments]. Smogorzewska EM, Weinberg KI, Kohn DB. Med Wieku Rozwoj; 2003 Nov; 7(1):27-34. PubMed ID: 13130167 [Abstract] [Full Text] [Related]
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14. Treatment of severe combined immunodeficiency disease (SCID) due to adenosine deaminase deficiency with CD34+ selected autologous peripheral blood cells transduced with a human ADA gene. Amendment to clinical research project, Project 90-C-195, January 10, 1992. Blaese RM, Culver KW, Chang L, Anderson WF, Mullen C, Nienhuis A, Carter C, Dunbar C, Leitman S, Berger M. Hum Gene Ther; 1993 Aug; 4(4):521-7. PubMed ID: 7691188 [Abstract] [Full Text] [Related]
16. A 24-Year Enzyme Replacement Therapy in an Adenosine-deaminase-Deficient Patient. Tartibi HM, Hershfield MS, Bahna SL. Pediatrics; 2016 Jan; 137(1):. PubMed ID: 26684479 [Abstract] [Full Text] [Related]
17. Treatment of patients with severe combined immunodeficiency due to adenosine deaminase (ADA) deficiency by autologous transplantation of genetically modified bone marrow cells. Hoogerbrugge PM, Vossen JM, v Beusechem VW, Valerio D. Hum Gene Ther; 1992 Oct; 3(5):553-8. PubMed ID: 1420454 [No Abstract] [Full Text] [Related]
18. Management options for adenosine deaminase deficiency; proceedings of the EBMT satellite workshop (Hamburg, March 2006). Booth C, Hershfield M, Notarangelo L, Buckley R, Hoenig M, Mahlaoui N, Cavazzana-Calvo M, Aiuti A, Gaspar HB. Clin Immunol; 2007 May; 123(2):139-47. PubMed ID: 17300989 [Abstract] [Full Text] [Related]
20. Biochemical and immunological status following gene therapy and PEG-ADA therapy for adenosine deaminase (ADA) deficiency. Fairbanks LD, Simmonds HA, Hoogerbrugge PM, van Beusechem VW, Valerio D, Moseley A, Levinsky RJ, Gaspar HB, Morgan G. Adv Exp Med Biol; 1994 May; 370():391-4. PubMed ID: 7660936 [No Abstract] [Full Text] [Related] Page: [Next] [New Search]